Duchenne Muscular Dystrophy Platform Trial
Stakeholder Meeting

Sheraton Silver Spring | Silver Spring, MD
September 9, 2019 | 8:30 AM - 5:00 PM


The Duchenne Platform Trial is being designed to increase access to therapeutic trials across the Duchenne community, with the goals of:

  • More rapid completion of testing and approval of new Duchenne therapies 
  • Reduced clinical trial start-up and execution time 
  • Enhanced patient experience, reduced number on placebo 
  • Potential for rapidly testing combination therapies 

The trial will study multiple drugs in multiple patient types with one common placebo-controlled arm.

The stakeholder meeting will be hosted by Parent Project Muscular Dystrophy, I-ACT for Children, and the Critical Path Institute.

Hotel Accommodations

PPMD has retained a discounted room rate at the Sheraton Silver Spring Hotel (8777 Georgia Ave., Silver Spring, MD, 20910). The group rate is $229 per night. Hotel blocks fill quickly, so we encourage you to book early to secure your room. The DEADLINE to make your reservation is Friday, August 30, 2019. Click here to book online.


Click here to view the draft agenda.

Not able to attend?

This meeting will be live streamed on our website for those unable to attend the event in person. If you would like to submit a question, please email your questions to elizabethh@parentprojectmd.org with the subject line "Duchenne Platform Trial Meeting" by September 4.


There is no fee for this event, but registration is required. The registration deadline is September 4, 2019.

We're sorry, the deadline for buying tickets for this event has passed.